International Niemann–Pick Disease Alliance

Updates

  1. ORPHAZYME ANNOUNCES INTERIM REPORT FIRST HALF 2019

    Copenhagen, Denmark, August 28, 2019 – Orphazyme A/S (ticker: ORPHA.CO), a biopharmaceutical company dedicated to developing treatments for patients living with rare diseases, today announces its interim financial results for the period January 1 – June 30, 2019 and corporate highlights. “We have made...

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  2. CTD Announces New Data Presented at Annual Gathering of Patients and Families Tackling Niemann-Pick Disease Type C

    CTD presentation to take place at the National Niemann-Pick Disease Foundation Conference August 16, 2019 ALACHUA, FL – (Businesswire) – August 14, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for...

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  3. Anders Hinsby: Letter to NP-C Community

    17 July 2019   Dear Global Community of NPC Patients, Families, Friends and Supporters,   I am writing to personally share the news that I will be resigning my position as Orphazyme’s Chief Executive Officer effective October 1, 2019....

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  4. CTD Appoints Head of Global Regulatory Affairs

    ALACHUA, FL – (BusinessWire) – July 08, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical need, today announced the appointment of Mr. Michael...

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  5. Orphazyme to prepare for filing of arimoclomol in Europe for Niemann-Pick disease Type C (NPC)

    Orphazyme to prepare for filing of arimoclomol in Europe for Niemann-Pick disease Type C (NPC) • Expected submission of Marketing Authorization Application (MAA) in H1 2020 Copenhagen, June 7, 2019 – Orphazyme A/S (ticker: ORPHA.CO), a biopharmaceutical company dedicated...

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  6. CTD Holdings Closes $7.4 Million Private Placement

    ALACHUA, FL / ACCESSWIRE / May 31, 2019 / CTD Holdings, Inc. (OTCQB: CTDH)(“CTD” or the “Company”), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical need, today announced that it closed...

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  7. CTD Announces Home-Based Dosing of First Patient in US Extension Protocol of Clinical Trial using Intravenous Administration of Trappsol® Cyclo™ for Niemann-Pick Disease Type C

    ALACHUA, FL – (Accesswire) – May 23, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical need, today announced its first home-based infusion of...

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  8. CTD Announces Participation and Support for Upcoming Gathering of Patient-Support Organizations for Niemann-Pick Disease type C

    ALACHUA, FL – (Accesswire) – May 16, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of disease with unmet medical need, today announced that company representatives will attend...

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  9. International Niemann Pick Disease Alliance – 6th Biennial “Face to Face” Meeting

    International Niemann Pick Disease Alliance 6th Biennial “Face to Face” Meeting 14-16 June 2019   Radisson Blu Hotel Lyon 129 Rue Servient, 69003 Lyon, France https://www.radissonblu.com/en/hotel-lyon   We are pleased to announce that the 6th Biennial INPDA Face-to-Face Meeting...

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  10. CTD Announces New Expanded Access Program in Taiwan using Trappsol® Cyclo™ for Niemann-Pick Disease type C

    Program is open to two patients who completed CTD’s clinical trial with Trappsol® Cyclo™ in the United States ALACHUA, FL – (Accesswire) – May 07, 2019 – CTD Holdings, Inc. (OTCQB: CTDH), a clinical stage...

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