International Niemann–Pick Disease Alliance
Orphazyme’s ‘Observational’ study for NP-C has been registered and made available on www.clinicaltrials.gov. The trial identifier is NCT02435030. Confirmed sites and contact details are provided.
https://clinicaltrials.gov/ct2/show/NCT02435030?term=arimoclomol&rank=5
You can find further information on Orphazyme’s website www.orphazyme.com