A global network of non-profit organisations supporting those affected by Niemann-Pick diseases. We’re under renovation, stay tuned!

IntraBio Receives European Commission Approval of AQNEURSA® for the Treatment of Niemann-Pick Type C Disease

AUSTIN, Texas–(BUSINESS WIRE)–IntraBio Inc. today announced that the European Commission granted marketing authorization to AQNEURSA® (levacetylleucine) for the treatment of...

Patient Information Sheet: NAVIGATE Phase 3 Clinical Trial

INPDA Global Niemann Pick Disease Initiatives

INPDA Global Niemann Pick Disease Initiatives INPDA is actively engaged in a number of initiatives and campaigns which  have...